CorLiCyte is a novel biologic treatment for Diabetic Foot Ulcers (DFUs) based on umbilical cord stem cell research. DFUs are open sores or wounds that may result from poor blood circulation or a lack of sensation due to nerve damage caused by elevated blood glucose levels. The regenerative effect of the stem cells can help to stop the inflammation, giving the blood vessels a chance to heal.

GLASSIA is a medicine containing human Alpha₁-Proteinase Inhibitor (Alpha₁-PI) also known as alpha₁-antitrypsin (AAT) and is used to treat adults with lung disease (emphysema) because of severe Alpha₁ antitrypsin (AAT) deficiency. GLASSIA is not meant to be used as a therapy in individuals with lung disease other than severe Alpha₁-PI deficiency.

Kigabeq® is a paediatric form of vigabatrin developed in breakable soluble tablets with two strengths (500mg and 100mg) for the treatment of infantile spasms (West syndrome). West syndrome is an extremely serious disease in infancy which progresses into major encephalopathy if untreated and for which vigabatrin is a key component of the treatment armamentarium.

Rybrila is indicated for the symptomatic treatment of severe sialorrhoea in children and adolescents aged 3 years and older with chronic neurological disorders. Sialorrhoea, also referred to as drooling or ptyalism, is the involuntary spillage of saliva from the mouth caused by excessive saliva production, inability to retain saliva in the mouth, or problems with swallowing

Raviten® (MTR-107) is an injectable solution of S-ethylisothiouronium diethylphosphate under development for the management of intradialytic hypotension. The drug has been shown in preclinical and exploratory clinical trials to normalize low blood pressure in patients suffering from Intradialytic Hypotension (IH), as well as other low blood pressure conditions. Raviten was the first drug designated with orphan drug designation by the FDA to the indication of intradialytic hypotension. Additionally, the drug was awarded with Fast Track designation by the FDA, acknowledging the importance of the treatment to End Stage Renal Disease (ESRD) patient.

Intradialytic Hypotension is a debilitating disease that deteriorate ESRD patients and associate with high risk of morbidity and mortality. There is no approve treatment of intradialytic hypotension as of date. There are approximately about 100,000 patient living with IH in the USA. The drug is currently about to enter adaptive phase IIB, and hopefully if proved effective can be a viable solution for IH rare disease community.

Teduglutide is a prescription medicine used in adults and children 1 year of age and older with short bowel syndrome (SBS) who are dependent on parenteral support. SBS is a serious and chronic malabsorption disorder that occurs when parts of the intestine are removed surgically and the remaining intestine may not be able to absorb enough nutrients from food and drink.